Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively
Start Date
12/28/2022
Completion Date
2/25/2040
Summary
A study to learn about the long-term safety and efficacy of giroctocogene fitelparvovec or fidanacogene elaparvovec in patients with hemophilia A or hemophilia B respectively, who have received treatment through prior participation in a Pfizer-sponsored clinical trial. Data collection and participant visits will be based on standard of care.
Eligibility Criteria
Age Range: 18 years to No maximum
Interventions
Testing of hepatic AAV Vector integration
Conditions
Locations
The Regents of the University of California||UC Davis Health
Rancho Cordova, California 95670
United States
UC Davis Health
Sacramento, California 95816
United States
UC Davis Ambulatory Care Clinic
Sacramento, California 95817
United States
UC Davis Hemophilia Treatment Center
Sacramento, California 95817
United States
UC Davis Medical Center
Sacramento, California 95817
United States
UCSF Outpatient Hematology Clinic
San Francisco, California 94143
United States
USF Health Morsani Center For Advanced Healthcare
Tampa, Florida 33612
United States
The University of South Florida Board of Trustees
Tampa, Florida 33620
United States
Mississippi Center For Advanced Medicine
Madison, Mississippi 39110
United States
Cornell University||Joan & Sanford I. Weill Medical College
New York, New York 10065
United States
Weill Cornell Medical College-New York Presbyterian Hospital
New York, New York 10065
United States
The Childrens Hospital of Philadelphia Division of Hematology
Philadelphia, Pennsylvania 19104
United States
The Childrens Hospital of Philadelphia Division of Hematology
Philadelphia, Pennsylvania 19146
United States
Washington Institute for Coagulation
Seattle, Washington 98101
United States
Royal Prince Alfred Hospital
Camperdown, New South Wales 2050
Australia
Sydney Local Health District (RPAH Zone)
Camperdown, New South Wales 2050
Australia
Unity Health Toronto, St. Michael's Hospital
Toronto, Ontario M5B 1W8
Canada
Kyung Hee University Hospital at Gangdong
Seoul, 05278
South Korea
Skåne University Hospital
Malmö, 21428
Sweden
Taichung Veterans General Hospital
Taichung, 40705
Taiwan
National Taiwan University Hospital
Taipei, 10041
Taiwan
Ege Universitesi Hastanesi
Izmir, İ̇zmir 35100
Turkey (Türkiye)
Acibadem Adana Hospital
Adana, 01130
Turkey (Türkiye)