Safety and Efficacy of 3 Dose Levels of NMD670 in Adult Patients With Myasthenia Gravis
Start Date
5/16/2024
Completion Date
12/1/2026
Summary
This Phase 2 proof-of-concept, dose range finding study aims to evaluate the safety and efficacy of 3 dose levels of NMD670 vs placebo in adult patients with MG with antibodies against AChR or MuSK, administered twice a day (BID) for 21 days.
Eligibility Criteria
Age Range: 18 years to No maximum
Interventions
NMD670
Placebo
Conditions
Locations
Profound Research LLC
Carlsbad, California 92011
United States
University of California Irvine Medical Center
Irvine, California 92868
United States
University of Colorado Neuromuscular Division
Aurora, Colorado 80045
United States
SFM Clinical Research, LLC
Boca Raton, Florida 33487
United States
Neuromuscular Research Division | University of South Florida
Tampa, Florida 33612
United States
Augusta University, Neuroscience Center
Augusta, Georgia 30912
United States
NextGen Precision Health
Columbia, Missouri 65212
United States
The University of North Carolina at Chapel Hill
Chapel Hill, North Carolina 27599
United States
The Ohio State University
Columbus, Ohio 43221
United States
University of Oregon
Portland, Oregon 97239
United States
Semmes Murphey Clinic
Memphis, Tennessee 38120
United States
UZ Leuven
Leuven,
Belgium
Aarhus University Hospital
Aarhus,
Denmark
Rigshospitalet University of Copenhagen
Copenhagen,
Denmark
Centre de référence des maladies neuromusculaires AOC-CHU de Bordeaux - Hôpital Pellegrin
Bordeaux,
France
Centre de Référence des Maladies Neuromusculaires et de la SLA
Marseille,
France
Centre Hospitalier Universitaire de Nantes - Hôtel Dieu Centre de Référence des Maladies Neuromusculaires Rares -
Nantes,
France
CHU de Nice
Nice,
France
Unité de Recherche Clinique NeuroSciences
Nice,
France
JSC Curatio
Tbilisi,
Georgia
LTD David Tatishvili Health Center
Tbilisi,
Georgia
Ltd New Hospitals
Tbilisi,
Georgia
ASST Papa Giovanni XXIII (Azienda Ospedaliera Papa Giovanni XXIII)
Bergamo, 21127
Italy
IRCCS Istituo delle Scienze neurologiche di Bologna, UOC Clinica neurologica Ospedale
Bologna, 40139
Italy
IRCCS Ospedale Policlinico San Martino
Genova, 16132
Italy
IRCCS Fondazione Istituto Neurologico Carlo Besta, Dipartimento di Ricerca e Sviluppo clinico
Milan, 20133
Italy
DIMER, IRCCS, Ospedale San Raffaele
Milan,
Italy
Centro Sclerosi Multipla Napoli - AOU Vanvitelli
Naples, 80138
Italy
AOU Pisana
Pisa, 56126
Italy
Azienda Ospedaliera Sant'Andrea - Universita di Roma La Sapienza
Roma, 00189
Italy
Leiden Universitair Medisch Centrum (LUMC)
Leiden, 2333
Netherlands
Neurologia Śląska Centrum Medyczne
Katowice,
Poland
Szpital Specjalistyczny im. Ludwika Rydygiera w Krakowie sp.z o.o
Krakow,
Poland
Centrum Medyczne Hope Clinic
Lublin, 20701
Poland
Galen Clinic
Lublin,
Poland
NeuroCor Banaszkiewicz, Tomaszewski Lekarze Spółka Partnerska
Myślenice,
Poland
Centrum Medyczne Neuro Protect
Warsaw,
Poland
University Clinical Center of Serbia, Neurology Clinic
Belgrade,
Serbia
University Clinical Center Nis, Neurology Clinic
Niš,
Serbia
Hospìtal Universitari Vall d'Hebrón
Barcelona,
Spain