NCT06925269Recruiting

DMD Voice: Qualitative Interviews With Patients and Caregivers

Red Nucleus Enterprise Solutions, LLC

Start Date

3/31/2025

Completion Date

12/1/2026

Summary

The purpose of this study is to understand DMD functional losses or abilities and their association with independence and quality of life from the perspective of individuals with DMD and/or and their caregivers. This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.

Eligibility Criteria

Age Range: 10 years to No maximum

Inclusion Criteria: Subsample A - Patients Eligible participants for Subsample A must: * Have been treated with Givinostat for at least 2 years * Be at least 10 years of age with signed consent of a parent or legal guardian * Be currently taking givinostat * Willing and able to participate in a video and/or audio recorded interview Subsample A - Caregivers Eligible caregivers for Subsample A must: * Be a parent or legal guardian of an individual with DMD that has been taking givinostat for at least two years * Willing and able to participate in a video and/or audio recorded interview Subsample B - Caregivers Eligible caregivers for Subsample B must: * Provide care to an individual with DMD who is unable to raise their hands above their head as confirmed by the caregiver * Reside in the United States or Canada * Able to read, speak, and understand English * Willing and able to participate in a video and/or audio recorded interview Have access to a stable internet connection Exclusion Criteria: \-

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Conditions

Duchenne Muscular Dystrophy (DMD)

Locations

Red Nucleus

Yardley, Pennsylvania 19067

United States