Study to Evaluate the Efficacy and Safety of Oral Rilzabrutinib in Adults With Immune Thrombocytopenia (ITP) Who Failed First-line Treatment
Start Date
10/24/2025
Completion Date
12/30/2028
Summary
This is a multinational, open label, single arm study that will evaluate the impact of early multi-immune modulation with rilzabrutinib in adult ITP patients who failed first-line treatment. The study includes a screening period (up to 8 weeks), a primary analysis period (up to 28 weeks), a long-term extension period for selected participants (28 weeks) and a 24-week follow-up period only for eligible participants.
Eligibility Criteria
Age Range: 18 years to No maximum
Interventions
rilzabrutinib
Conditions
Locations
Community Health Partners (CHP) - Community Medical Oncology Specialists (University Oncology Associates)
Clovis, California 93611
United States
University of Southern California (USC)
Los Angeles, California 90089
United States
Tulane University Health Sciences Center - Tulane Avenue-Investigational Site Number: 8400011
New Orleans, Louisiana 70112
United States
Massachusetts General Hospital Cancer Center
Boston, Massachusetts 02114
United States
Beth Israel Deaconess Medical Center
Boston, Massachusetts 02215
United States
Mass General Brigham Cancer Institute
Danvers, Massachusetts 01923
United States
University of Michigan Health - Michigan Medicine - University Hospital-Investigational Site Number: 8400001
Ann Arbor, Michigan 48109
United States
Mayo Clinic_Investigational Site Number: 8400009
Rochester, Minnesota 55905
United States
New York Oncology Hematology-Investigational Site Number: 8400010
Albany, New York 12208
United States
Montefiore Medical Center-Investigational Site Number: 8400012
The Bronx, New York 10467
United States
Oregon Health and Sciences University
Portland, Oregon 97239
United States
Community Cancer Trials of Utah-Investigational Site Number: 8400002
Ogden, Utah 84405
United States
Investigational Site Number : 0400001
Vienna, 1140
Austria
Investigational Site Number : 2030002
Prague, 12800
Czechia
Investigational Site Number: 2500003
Créteil, 94000
France
Investigational Site Number : 2500001
Dijon, 21079
France
Investigational Site Number : 2500002
Pessac, 33604
France
Investigational Site Number : 2500004
Toulouse, 31059
France
Investigational Site Number : 2760004
Leipzig, 04103
Germany
Investigational Site Number : 3480001
Budapest,
Hungary
Investigational Site Number : 3480002
Kaposvár, 7400
Hungary
Investigational Site Number : 3800002
Meldola,
Italy
Investigational Site Number : 3800004
Milan, 20162
Italy
Investigational Site Number : 3800006
Naples, 80131
Italy
Investigational Site Number : 3800007
Torino, 10126
Italy
Investigational Site Number : 3800003
Vicenza, 36100
Italy
Investigational Site Number : 6160002
Gdansk, 80-219
Poland
Investigational Site Number : 6160003
Skorzewo, 60-185
Poland
Investigational Site Number : 6160004
Słupsk, 76-200
Poland
Investigational Site Number : 7240001
Barcelona, 8003
Spain
Investigational Site Number : 7240002
Burgos, 9006
Spain
Investigational Site Number : 7240007
Madrid, 28007
Spain
Investigational Site Number : 7240008
Madrid, 28046
Spain
Investigational Site Number : 7240005
Murcia, 30008
Spain
Investigational Site Number : 7240003
San Cristóbal de La Laguna,
Spain
Investigational Site Number : 7240004
Seville, 41013
Spain