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NCT04561518Recruiting

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

Alnylam Pharmaceuticals

Start Date

11/23/2020

Completion Date

12/31/2033

Summary

The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients * Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting * Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant

Eligibility Criteria

Age Range: No minimum to No maximum

Inclusion Criteria: * Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant for the cohort of pre-symptomatic carriers * Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis Exclusion Criteria: * Current enrollment in a clinical trial for any investigational agent

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Conditions

Transthyretin-Mediated AmyloidosisATTR Amyloidosis

Locations

Clinical Trial Site

La Jolla, California 92037

United States

Clinical Trial Site

Los Angeles, California 90095

United States

Clinical Trial Site

Jacksonville, Florida 32224

United States

Clinical Trial Site

Iowa City, Iowa 52242

United States

Clinical Trial Site

Kansas City, Kansas 66160

United States

Clinical Trial Site

Baltimore, Maryland 21224

United States

Clinical Trial Site

Boston, Massachusetts 02127

United States

Clinical Trial Site

New York, New York 10034

United States

Clinical Trial Site

Durham, North Carolina 27710

United States

Clinical Trial Site

Columbus, Ohio 43210

United States

Clinical Trial Site

Philadelphia, Pennsylvania 19104

United States

Clinical Trial Site

Austin, Texas 78756

United States

Clinical Trial Site

Houston, Texas 77030

United States

Clinical Trial Site

Salvador,

Brazil

Clinical Trial Site

São Paulo,

Brazil

Clinical Trial Site

Sofia,

Bulgaria

Clinical Trial Site

Aarhus,

Denmark

Clinical Trial Site

Copenhagen,

Denmark

Clinical Trial Site

Bordeaux,

France

Clinical Trial Site

Bron,

France

Clinical Trial Site

Créteil,

France

Clinical Trial Site

Le Kremlin-Bicêtre,

France

Clinical Trial Site

Marseille,

France

Clinical Trial Site

Berlin,

Germany

Clinical Trial Site

Giessen,

Germany

Clinical Trial Site

Hanover,

Germany

Clinical Trial Site

Jerusalem,

Israel

Clinical Trial Site

Ramat Gan,

Israel

Clinical Trial Site

Milan,

Italy

Clinical Trial Site

Naples,

Italy

Clinical Trial Site

Palermo,

Italy

Clinical Trial Site

Roma,

Italy

Clinical Trial Site

Groningen,

Netherlands

Clinical Trial Site

Lisbon,

Portugal

Clinical Trial Site

Porto,

Portugal

Clinical Trial Site

Barcelona,

Spain

Clinical Trial Site

Madrid,

Spain

Clinical Trial Site

Palma,

Spain

Clinical Trial Site

New Taipei City,

Taiwan

Clinical Trial Site

Taipei,

Taiwan