ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
Start Date
11/23/2020
Completion Date
12/31/2033
Summary
The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients * Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting * Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant
Eligibility Criteria
Age Range: No minimum to No maximum
Conditions
Locations
Clinical Trial Site
La Jolla, California 92037
United States
Clinical Trial Site
Los Angeles, California 90095
United States
Clinical Trial Site
Jacksonville, Florida 32224
United States
Clinical Trial Site
Iowa City, Iowa 52242
United States
Clinical Trial Site
Kansas City, Kansas 66160
United States
Clinical Trial Site
Baltimore, Maryland 21224
United States
Clinical Trial Site
Boston, Massachusetts 02127
United States
Clinical Trial Site
New York, New York 10034
United States
Clinical Trial Site
Durham, North Carolina 27710
United States
Clinical Trial Site
Columbus, Ohio 43210
United States
Clinical Trial Site
Philadelphia, Pennsylvania 19104
United States
Clinical Trial Site
Austin, Texas 78756
United States
Clinical Trial Site
Houston, Texas 77030
United States
Clinical Trial Site
Salvador,
Brazil
Clinical Trial Site
São Paulo,
Brazil
Clinical Trial Site
Sofia,
Bulgaria
Clinical Trial Site
Aarhus,
Denmark
Clinical Trial Site
Copenhagen,
Denmark
Clinical Trial Site
Bordeaux,
France
Clinical Trial Site
Bron,
France
Clinical Trial Site
Créteil,
France
Clinical Trial Site
Le Kremlin-Bicêtre,
France
Clinical Trial Site
Marseille,
France
Clinical Trial Site
Berlin,
Germany
Clinical Trial Site
Giessen,
Germany
Clinical Trial Site
Hanover,
Germany
Clinical Trial Site
Jerusalem,
Israel
Clinical Trial Site
Ramat Gan,
Israel
Clinical Trial Site
Milan,
Italy
Clinical Trial Site
Naples,
Italy
Clinical Trial Site
Palermo,
Italy
Clinical Trial Site
Roma,
Italy
Clinical Trial Site
Groningen,
Netherlands
Clinical Trial Site
Lisbon,
Portugal
Clinical Trial Site
Porto,
Portugal
Clinical Trial Site
Barcelona,
Spain
Clinical Trial Site
Madrid,
Spain
Clinical Trial Site
Palma,
Spain
Clinical Trial Site
New Taipei City,
Taiwan
Clinical Trial Site
Taipei,
Taiwan