Back to Trials
NCT07116031PHASE2Recruiting

A Study of Belumosudil in Children With Chronic Graft Versus Host Disease (schoolROCK)

Sanofi

Start Date

12/2/2025

Completion Date

2/28/2031

Summary

This is an open-label, single group, Phase 1/2, 1-arm study for treatment of children aged 1 to \<18 years with active moderate-to-severe cGVHD that is refractory to or recurred after at least 2 prior lines of systemic therapy for cGVHD. The purpose of Phase 1 is to determine the PK profiles and to establish the Recommended Pediatric Equivalent Dose (RPED) of belumosudil in participants aged 1 to \<12 years with active moderate to severe cGVHD. Upon completion and evaluation of Phase 1, Phase 2 will commence with the purpose of determining safety and efficacy (ORR by 24 weeks) of belumosudil in participants aged 1 to \<18 years. Study details include: The end of study is defined as 3 years after the last participant is recruited or all participants have discontinued treatment, or have died, whichever comes first. Minimum of 6 participants ages 1 to 6 years will be enrolled for each phase of study Individual participant duration on study will consist of: Up to 4 weeks for screening. Treatment until clinically significant progression of cGVHD, relapse/recurrence of the underlying disease, start of a new systemic treatment for cGVHD, experience of an unacceptable adverse event, request from participant or Investigator, or until the end of the study is reached, whichever comes first. 30 days of post treatment safety follow-up. Long-term follow-up until death or end of study, whichever occurs first.

Eligibility Criteria

Age Range: 1 years to 18 years

Inclusion Criteria: * Participant must be 1 to \<18 years of age, at the time the consent/assent is signed. For Phase 1: participant must be 1 to \<12 years of age, at the time the consent/assent is signed. For Phase 2: participant must be 1 to \<18 years of age, at the time the consent/assent is signed. * Participant has undergone an allogeneic HCT * Has active moderate to severe cGVHD, defined using the NIH Consensus diagnosis and staging criteria for which systemic therapy is required * cGVHD is refractory to or has recurred after at least 2 prior lines of systemic treatment * Has received at least two lines of prior systemic therapy for cGVHD, but no more than 5 lines. * If participant receives corticosteroid therapy for cGVHD, the dose must be stable for at least 2 weeks prior to the first dose of the IMP * Has a Lansky-Play (if aged \<16 years) or Karnofsky (if aged ≥16 years) performance scale of ≥60 * Body weight of 8 kg and above * Contraceptive use by sexually active male and female should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies * The participant or their legally authorized representative (LAR) must be capable of giving signed informed consent * Life expectancy of \>6 months * Participants can take the IMP orally or via a nasogastric tube Exclusion Criteria: * Progressive underlying disease or post-transplant lymphoproliferative disease within 4 weeks prior to the first dose of the IMP. * Diagnosed with another malignancy (other than malignancy for which transplant was performed) within 3 years prior to the first dose of the IMP * History or other evidence of severe illness or any other conditions that would make the participant, in the opinion of the Investigator, unsuitable for the study (such as malabsorption syndromes, active, uncontrolled infections, or poorly controlled psychiatric disease) * Has a forced expiratory volume (in the first second; FEV1) ≤39% or has lung score of 3 * Female participants who are pregnant or breastfeeding * Participants who meet any of the following criteria regarding systemic GVHD treatments: * Participants who newly initiated any systemic GVHD treatment within 14 days prior to the first dose of belumosudil. * Participants receiving systemic GVHD treatments ibrutinib, ruxolitinib, mycophenolate (MMF), methotrexate, rituximab, axatilimab, or imatinib who are unable to meet the following requirements: * No dose increases from 14 days prior to belumosudil initiation and continuing for the first 14 days of belumosudil treatment (dose reductions and discontinuations are permitted during this period) * Ability to discontinue these therapies within 14 days after initiating belumosudil (allowing for a maximum overlap period of up to 14 days with belumosudil treatment) * Participants receiving other systemic GVHD treatments (apart from corticosteroids and calcineurin inhibitors) including investigational treatments who have not completed a washout period of at least 28 days or 5 half-lives (whichever is shorter) prior to the first dose of belumosudil. No washout period is required for extracorporeal photopheresis (ECP) or sirolimus therapy, but these must be discontinued before study treatment initiation. Note: Corticosteroids and calcineurin inhibitors may continue throughout the study. * The use of herbal and recreational drugs within 7 days before the start of study intervention * Participant has had previous exposure to belumosudil * Administration of live or live-attenuated vaccines is prohibited within 28 days or 5 elimination half-lives of the respective vaccine, whichever is longer, prior to IMP administration and until study intervention discontinuation * Treatment with any non-GVHD investigational agent, or any investigational device or procedure, within 28 days (or 5 half-lives, whichever is longer) of enrollment, prior to the first dose of the IMP * For Phase 1 only: Administration with strong CYP3A4 inducers is not allowed within 14 days or 5 half-lives (whichever is longer) of the first dose of IMP until the study intervention discontinuation. * For Phase 1 only: PPIs are not allowed within 1 day or 5 half-lives (whichever is longer) of the first dose of IMP and Day 15 of Cycle 1. They can be restarted on Cycle 1 Day 16. * Absolute neutrophil count \<1.0 × 109/L. The use of granulocyte-colony stimulating factor (G-CSF) is not allowed within 7 days prior to the ANC test to reach this level during screening * Platelet count \<25 × 109/L. Platelet transfusions are not allowed within 72 hours before hematology screening test. Participants with platelet transfusion refractoriness will be excluded. (Participants who have suboptimal responses to at least 2 transfusions will be considered as platelet transfusion refractory) * Alanine aminotransferase (ALT) and/or aspartate aminotransferase (AST) \>3× upper limit of normal (ULN) (\> 5x ULN if abnormalities are due to cGVHD) * Total bilirubin \>1.5 × ULN (\>3 x ULN if Gilbert's syndrome or if abnormalities are due to cGVHD) * Glomerular filtration rate (GFR) \<30 mL/min/1.73 m2 using the revised Bedside Schwartz calculator * Participants with an active viral disease including hepatitis B virus (HBV) and hepatitis C virus (HCV) * Active uncontrolled Cytomegalovirus (CMV) or Epstein-Barr virus (EBV) infection * Known history of human immunodeficiency virus (HIV) * Not suitable for participation, whatever the reason, as judged by the Investigator, including medical or clinical conditions, or participants potentially at risk of noncompliance to study procedures The above information is not intended to contain all considerations relevant to a patient's potential participation in a clinical trial.

Interventions

DRUG

Belumosudil

DRUG

Belumosudil

Interested in This Trial?

Contact the trial locations directly using the information below to learn more about enrollment.

Expressing interest lets you review the study and consent before we connect you with the research site.

Conditions

Chronic Graft Versus Host Disease

Locations

Children's Hospital Los Angeles- Site Number : 8400009

Los Angeles, California 90027

United States

Children's National Medical Center - Washington- Site Number : 8400005

Washington D.C., District of Columbia 20010

United States

Memorial Sloan Kettering Cancer Center - New York - York Avenue- Site Number : 8400001

New York, New York 10065

United States

Texas Children's Hospital- Site Number : 8400008

Houston, Texas 77030

United States

Fred Hutchinson Cancer Research Center- Site Number : 8400002

Seattle, Washington 98109

United States

Investigational Site Number : 0560003

Ghent, 9000

Belgium

Investigational Site Number : 0560001

Leuven, 3000

Belgium

Investigational Site Number : 1240001

Vancouver, British Columbia V6H 3N1

Canada

Investigational Site Number : 1240002

Toronto, Ontario M5G 1X8

Canada

Investigational Site Number : 1560003

Beijing, 100045

China

Investigational Site Number : 1560001

Shanghai, 200040

China

Investigational Site Number : 1560004

Shenzhen, 518026

China

Investigational Site Number : 1560002

Suzhou, 215025

China

Investigational Site Number : 2500002

Marseille, 13885

France

Investigational Site Number : 2500001

Paris, 75019

France

Investigational Site Number : 2760001

Berlin, 13353

Germany

Investigational Site Number : 3760005

Haifa, 3109601

Israel

Investigational Site Number : 3760002

Jerusalem, 9112001

Israel

Investigational Site Number : 3760004

Petah Tikva, 4920235

Israel

Investigational Site Number : 3760003

Ramat Gan, 5262100

Israel

Investigational Site Number : 3760001

Tel Aviv, 6423906

Israel

Investigational Site Number : 3800002

Milan, Milano 20122

Italy

Investigational Site Number : 3800001

Rome, Roma 00165

Italy

Investigational Site Number : 3800003

Turin, Torino 10126

Italy

Investigational Site Number : 3920002

Tokyo, 157-8535

Japan

Investigational Site Number : 5280001

Utrecht, 3584 CS

Netherlands

Investigational Site Number : 7240003

Esplugues de Llobregat, Barcelona [Barcelona] 08950

Spain

Investigational Site Number : 7240001

Barcelona, 08035

Spain

Investigational Site Number : 7240002

Madrid, 28009

Spain

Investigational Site Number : 7920003

Ankara, 06800

Turkey (Türkiye)

Investigational Site Number : 7920001

Izmir, 35100

Turkey (Türkiye)

Investigational Site Number : 8260002

Newcastle upon Tyne, England NE2 4HH

United Kingdom

Investigational Site Number : 8260001

London, London, City of WC1N 3JH

United Kingdom